Gene Therapy Research Institution Co., Ltd.

Development of gene therapy

Using adeno-associated virus (AAV) as a vector to carry therapeutic genes, we are developing gene therapy for intractable diseases for which no effective treatment has been available so far. We have already started clinical trials for AADC deficiency, Parkinson's disease, and amyotrophic lateral sclerosis (ALS).

電話アイコン +81-44-400-1290


Regenerative Medicine

  • Drug Discovery/Drug Discovery Support